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Consensus reporting guidelines to address gaps in descriptions of ultra-rare genetic conditions
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J.G.G. is a consultant for Neurocrine, Shire-Takeda and Ionis Pharmaceuticals. J.F.B. is a full-time employee of Ionis Pharmaceuticals. S.T.C. holds founder stock in Ionis Pharmaceuticals.
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Gleeson, J.G., Bennett, C.F., Carroll, J.B. et al. Personalized antisense oligonucleotides ‘for free, for life’ — the n-Lorem Foundation. Nat Med 29, 1302–1303 (2023). https://doi.org/10.1038/s41591-023-02335-2
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DOI: https://doi.org/10.1038/s41591-023-02335-2
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